Urea Cycle Disorders Treatment Market Growth Forecast: Exploring Trends and Opportunities for the Next Decade
Updated 2025 Market Reports Released: Trends, Forecasts to 2034 – Early Purchase Your Competitive Edge Today!
How has the urea cycle disorders treatment market size evolved in recent years?
The market for the treatment of urea cycle disorders has been expanding consistently in the past few years. The projected growth suggests an increment from $1.33 billion in 2024 to $1.39 billion in 2025, equating to a compound annual growth rate (CAGR) of 4.0%. This growth in the historical period is a result of increased awareness and education, enhancements in newborn screening processes, the development of patient support networks and the establishment of standard care guidelines.
What are the predictions for the urea cycle disorders treatment market size in the coming years?
Over the next few years, the market for urea cycle disorders treatment is expected to expand consistently, with projections indicating a value of $1.65 billion by 2029. This predicted growth, occurring at a compound annual growth rate (CAGR) of 4.5%, is largely due to advances made in enzyme replacement therapy, the expansion of newborn screening programs, increased collaboration in research as well as the development of additional therapeutic options, and the utilization of telemedicine and remote care. Furthermore, anticipated trends within the forecast period encompass advanced gene editing techniques, regenerative medicine methodologies, initiatives aimed at increasing awareness and advocacy, studies focusing on long-term safety and efficacy, and the implementation of tailored nutritional therapies.
Get your urea cycle disorders treatment market report here!
What key factors are fueling the growth of the urea cycle disorders treatment market?
The increasing incidence of urea cycle disorders is anticipated to boost the growth of the market for its treatment. Urea cycle disorders are inherited metabolic disorders caused by defects in the enzymes or transporter molecules required to remove ammonia from the blood in the liver. The growth in the incidence of such disorders is fueled by genetic aberrations. If urea cycle disorder is identified as the cause of ammonia accumulation, a tailored treatment approach involving dietary regulation, medication, and monitoring can be employed to control and reduce its adverse effects. For example, StatPearls Publishing LLC, a medical education library based in the U.S., noted in April 2023 that the incidence of urea cycle disorders due to ornithine transcarbamylase deficiency was 1 in 140,000 individuals. Additionally, Lecturio, a digital medical education platform based in Germany, stated in September 2022 that urea cycle disorders (UCDs) affect around 1 in every 35,000 live births worldwide and 1 in 8,200 live births in the U.S., leading to an annual incidence of around 113 new cases in the U.S. and about 149 in Europe. Hence, the increasing incidence of urea cycle disorders is spurring the growth of the market for its treatment.
How is the global urea cycle disorders treatment market divided into key segments?
The urea cycle disorders treatment market covered in this report is segmented –
1) By Treatment: Amino Acid Supplements, Sodium Phenylbutyrate, Glycerol Phenylbutyrate, Sodium Benzoate, Other Treatments
2) By Enzyme Deficiency: Ornithine Transcarbamylase (OTC), Argininosuccinate Synthetase (AS), Arginase (AG), Argininosuccinate Lyase (AL), Carbamoyl Phosphate Synthase (CPS1)
3) By Route of Administration: Oral, Injectables
4) By Distribution Channel: Hospital Pharmacies, Retail Pharmacies, Online Pharmacies
Subsegments:
1) By Amino Acid Supplements: Arginine Supplements, Citrulline Supplements, Other Essential Amino Acids
2) By Sodium Phenylbutyrate: Powder Form, Tablet Form
3) By Glycerol Phenylbutyrate: Oral Solutions, Other Forms
4) By Sodium Benzoate: Intravenous Solutions, Oral Formulations
5) By Other Treatments: Liver Transplantation, Dietary Modifications, Enzyme Replacement Therapy, Other Supportive Therapies
Get your free sample now – explore exclusive market insights:
https://www.thebusinessresearchcompany.com/sample.aspx?id=12237&type=smp
Who are the key firms paving the way for growth in the urea cycle disorders treatment market?
Major companies operating in the urea cycle disorders treatment market include Bausch Health Companies Inc., Recordati Rare Diseases, Eurocept Pharmaceuticals Holding (Lucane Pharma SA), Acer Therapeutics, Ultragenyx Pharmaceutical, Aeglea BioTherapeutics, Arcturus Therapeutics, Inc., Orpharma Pty Ltd., Selecta Biosciences, Inc., Abbott Laboratories, Mead Johnson & Company, LLC, Horizon Therapeutics Plc, Nestlé S.A., Danone S.A., Biophone, Relief Therapeutics Holding AG, TheraTriage, Genomatica, Protalix BioTherapeutics, Erytech Pharma, 4D Pharma, Synlogic, Amicus Therapeutics, Sobi, Astellas Pharma Inc., Chiesi Farmaceutici S.p.A., Medpace Holdings, Inc., Celerion, and PTC Therapeutics
Which trends are expected to transform the urea cycle disorders treatment market?
The emergence of product innovation is a dominant trend spotted in the urea cycle disorder treatment market. Top-tier companies engaged in the sector are focusing on the development of groundbreaking products to firm their hold in the market. For example, Medunik USA, an enterprise located in the US and specializing in the pharmaceutical sector, launched Pheburane oral pellets in September 2022. This unique formulation of sodium phenylbutyrate (NaPB) masks flavor and is designed to manage urea cycle disorders in the long term. This prescription drug is designed to work alongside a specific diet to treat urea cycle disorders related to carbamyl phosphate synthetase (CPS), ornithine transcarbamylase (OTC), or argininosuccinate synthetase (AS) insufficiency in both children and adults. Each package contains a reusable, calibrated dosing spoon for measurement, thus differing from other NaPB forms that frequently require mixing or oral intake. Pheburane is versatile and can be consumed along with a meal or snack, or it can be imparted onto apple sauce or carrot puree and combined with water, fruit juice, or protein-free infant formula for intake.
Unlock exclusive market insights – purchase your research report now for a swift delivery!
https://www.thebusinessresearchcompany.com/purchaseoptions.aspx?id=12237
What regions are contributing significantly to the growth of the urea cycle disorders treatment market?
North America was the largest region in the urea cycle disorders treatment market in 2024. The regions covered in the urea cycle disorders treatment market report are Asia-Pacific, Western Europe, Eastern Europe, North America, South America, Middle East, Africa.
Browse Through More Similar Reports By The Business Research Company:
Power Generators Global Market Report 2023
https://www.thebusinessresearchcompany.com/report/power-generators-global-market-report
Silent Generator Global Market Report 2024
https://www.thebusinessresearchcompany.com/report/silent-generator-global-market-report
Diesel Generator Global Market Report 2024
https://www.thebusinessresearchcompany.com/report/diesel-generator-global-market-report
About The Business Research Company:
With over 15000+ reports from 27 industries covering 60+ geographies, The Business Research Company has built a reputation for offering comprehensive, data-rich research and insights. Armed with 1,500,000 datasets, the optimistic contribution of in-depth secondary research, and unique insights from industry leaders, you can get the information you need to stay ahead in the game.
Contact us at:
The Business Research Company: https://www.thebusinessresearchcompany.com/
Americas +1 3156230293
Asia +44 2071930708
Europe +44 2071930708
Email us at [email protected]
Follow us on:
LinkedIn: https://in.linkedin.com/company/the-business-research-company
YouTube: https://www.youtube.com/channel/UC24_fI0rV8cR5DxlCpgmyFQ
Global Market Model: https://www.thebusinessresearchcompany.com/global-market-model
Found this article helpful? Share it on:
